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Nusinersen for treating spinal muscular atrophy

  • Technology appraisal guidance
  • Reference number: TA588
  • Published:  24 July 2019
  • Guidance
  • Tools and resources
  • Information for the public
  • Evidence
  • History

On this page

  1. Declaration of interests
  2. Final draft guidance: 2
  3. Final draft guidance
  4. Draft guidance: 1
  5. Invitation to participate

History

Documents created during the development process.

Declaration of interests

  • Register of interests (PDF 142 KB)

    Published:
    27 July 2019

Final draft guidance: 2

  • Final draft guidance: 2

  • Final appraisal document (PDF 344 KB)

    Published:
    03 July 2019
  • Committee papers Managed Access Agreement (PDF 553 KB)

    Published:
    03 July 2019

Final draft guidance

  • Final draft guidance

  • Final appraisal document (PDF 338 KB)

    Published:
    03 June 2019
  • Committee papers (PDF 5.4 MB)

    Published:
    04 June 2019
  • Public committee slides (PDF 1.22 MB)

    Published:
    03 June 2019
  • Committee papers Draft Managed Access Agreement (PDF 559 KB)

    Published:
    03 June 2019

Draft guidance: 1

  • Draft guidance: 1

  • Appraisal consultation document (PDF 454 KB)

    Published:
    14 August 2018
  • Public committee slides (PDF 1.28 MB)

    Published:
    14 August 2018
  • Committee papers (PDF 15.7 MB)

    Published:
    14 August 2018

Invitation to participate

  • Final scope (PDF 244 KB)

    Published:
    18 January 2018
  • NICE's response to comments on the draft scope and provisional matrix (PDF 694 KB)

    Published:
    18 January 2018
  • Equality Impact Assessment (Guidance development) (PDF 174 KB)

    Published:
    18 January 2018
  • Final matrix (PDF 255 KB)

    Published:
    18 January 2018
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