Cipaglucosidase alfa with miglustat for treating late-onset Pompe disease

Equality Impact Assessment (Guidance development) (PDF 180 KB)

Final draft guidance

Final draft guidance (PDF 240 KB)

Committee papers (PDF 7.75 MB)

Final scope (PDF 184 KB)

NICE's response to comments on the draft scope and provisional stakeholder list (PDF 366 KB)

Equality impact assessment (Scoping) (PDF 133 KB)

Topic selection

Draft scope post referral (PDF 199 KB)